Muscle-specific CRISPR/Cas9 editing of the dystrophin gene ameliorates pathophysiology in a mouse model of Duchenne Muscular Dystrophy
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下载链接:
https://www.ncbi.nlm.nih.gov/bioproject/PRJNA358248
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资源简介:
Here we demonstrate successful in vivo gene editing of the dystrophin gene in a mouse model of Duchenne muscular dystrophy following AAV-mediated delivery of CRISPR/Cas9.
创建时间:
2016-12-20



