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In vivo liver-specific knock-in using low-dose AAV-CRISPR restored hemostasis in adult and neonatal hemophilia B mice

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NIAID Data Ecosystem2026-03-13 收录
下载链接:
https://www.ncbi.nlm.nih.gov/bioproject/PRJNA782865
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资源简介:
This study aims to restore hemostasis in adult and neonatal hemophilia B mice through in vivo liver-specific knock-in using low-dose AAV CRIPSR techonology
创建时间:
2021-11-23
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