List of AO compounds, the sequence and size of AOs and the summary of their exon skipping effect.

PS, 2OMePS AO. − and + within the Target column indicate the intron and exon sequences respectively; the numbers represent the first and last nucleotides of the oligonucleotide sequences. Percentage of GFP positive cells with 2OMePS AOs is the average from the flow cytometry analysis. Results from PMO treatment are presented as mean values ± SE with statistical analysis (ANOVA) since a completed set of exon skipping efficiency analysis including the in vivo test was conducted with those PMOs.*Pmdx mice were treated with 10 µg Vivi-PMO.