Target sequences and in vitro activity of CompoZr ZFNs.
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a: Spacer sequences are shown in lower case letters in italics. Bold letters denote polymorphic sites. Underlined letters denote the splice site. Lower case letters denote nucleotides flanking the left and right ZFN recognition sequences and gaps between adjacent ZFPs.b: in vitro activity was measured by Mel1 reporter assay and required at >50% except for cbfb where zebrafish SJD.1 cells were transfected and activity was measured by surveyor assay (>1% required).
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2015-12-02



