Muscle-specific CRISPR/Cas9 editing of the dystrophin gene ameliorates pathophysiology in a mouse model of Duchenne Muscular Dystrophy
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资源简介：
Here we demonstrate successful in vivo gene editing of the dystrophin gene in a mouse model of Duchenne muscular dystrophy following AAV-mediated delivery of CRISPR/Cas9.
创建时间：
2017-02-15
