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资源简介：
Sequencing data for capsid engineering of AAV9 to MyoAAV
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创建时间：
2021-08-15
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Stable alphavirus packaging cell lines for Sindbis virus- and Semliki Forest virus-derived vectors
Alphavirus vectors are being developed for possible human vaccine and gene therapy applications. We have sought to advance this field by devising DNA-based vectors and approaches for the production of
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An efficacious and safe rescue of GM3 synthase deficiency in mice by spatially regulated AAV-mediated ST3GAL5 delivery. An efficacious and safe rescue of GM3 synthase deficiency in mice by spatially regulated AAV-mediated ST3GAL5 delivery
The first-generation rAAV-ST3GAL5 replacement vector employing a ubiquitous promoter led to hepatic injury and death caused by high off-target ST3GAL5 expression when administered systemically. In con
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In vivo promoter biopanning with AAV
Recombinant Adeno-associated viruses (AAV) are flagship vectors for in vivo human gene therapy. An integral vector element are promoters, which control transgene expression in either a ubiquitous or c
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Single-cell transcriptomics of transfection-based rAAV production in HEK293 cells
Bulk and single-cell whole transcriptome analysis of adherent and suspension cultures of HEK293 cells during transfection-based rAAV9 production.
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