Dataset from An Open-Label Extension Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Patients With Type 1 Gaucher Disease
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下载链接：
https://doi.org/10.25934/00007248
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资源简介：
The purpose of this study is to evaluate the long-term safety of every other week dosing of
Gene-Activated® human glucocerebrosidase (GA-GCB, velaglucerase alfa) intravenously in
patients with type 1 Gaucher disease.
创建时间：
2024-11-26
