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NGS data of using Cpf1 to treat PH1
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创建时间：
2022-04-19
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in vivo NGS data for "Engineered PsCas9 enables therapeutic genome editing in mouse liver with lipid nanoparticles "
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WB original data (Efficient exon skipping by base editor-mediated abrogation of exonic splicing enhancers)
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Base editing mediated correction of severe Ã0 thalassemia mutations.
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