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Efficient rescue of retinal degeneration in Pde6a mice by all-in-one AAV-mediated Nrl gene inactivation

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NIAID Data Ecosystem2026-05-02 收录
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Here, we demonstrate that all-in-one AAV-SaCas9-mediated Nrl gene inactivation can efficiently prevent retinal degeneration in a RP mouse model with Pde6a mutation.

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2024-06-08
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