Patient-specific human induced pluripotent stem cells (hiPSCs) offer unprecedented opportunities for the investigation of multigenic disease, personalized medicine, and stem cell therapy. For heteroge

NIAID Data Ecosystem50

Base editor mediated correction of a tau mutation rescues cognitive decline in a mouse model of Alzheimers disease. Homo Sapiens

基因编辑治疗

阿尔茨海默病模型

Low sequence reads

NIAID Data Ecosystem30

Adenine base editing in mouse embryos and an adult mouse model of Duchenne muscular dystrophy

基因编辑治疗

肌营养不良模型

Measurement of base substitution induced by adenine base editor

NIAID Data Ecosystem50

Treatment of a metabolic liver disease by in vivo prime editing in mice

基因编辑治疗

代谢性肝病

Prime editing is a highly versatile CRISPR-based genome editing technology with the potential to correct the vast majority of genetic defects1. However, correction of a disease phenotype in vivo in so

NIAID Data Ecosystem40

High-throughput sequencing data of eeCas9 and eeBE of file7

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