5q-Spinal muscular atrophy (SMA) is a severely disabling inherited neuromuscular disease that progressively reduces the motor abilities of affected individuals. The approval of the antisense oligonucl

NIAID Data Ecosystem50

脊髓性肌萎缩症治疗评估

MRI磁共振成像

Excel file with raw data of muscle fat fraction before and after nusinersen treatment

Zenodo2023-02-28 更新20

dataset relate to article "Quality of life assessment in adult spinal muscular atrophy patients treated with nusinersen"

脊髓性肌萎缩症治疗评估

患者生活质量

Excel file with raw data of the INQoL scale scores for each domain, for each patient, before and after nusinersen treatment

NIAID Data Ecosystem70

dataset relate to article "Quality of life assessment in adult spinal muscular atrophy patients treated with nusinersen"

脊髓性肌萎缩症治疗评估

患者生活质量

Excel file with raw data of the INQoL scale scores for each domain, for each patient, before and after nusinersen treatment

Zenodo2023-02-23 更新30

Evidence matrix for SMA hypothetical treatment scenarios.

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