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资源简介：
Whole-genome sequencing for determining off-target
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创建时间：
2020-01-01
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rAAV9 integration in C57BL/6:C129 mus musculus
Neonatal mice were treated with an rAAV9 gene therapy vector, some of whom later developed tumors. We sampled the tumors of these mice, as well as the livers of two additional mice that did not have v
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Analyzing the Number of Common Integration Sites of Viral Vectors – New Methods and Computer Programs
Vectors based on γ-retroviruses or lentiviruses have been shown to stably express therapeutical transgenes and effectively cure different hematological diseases. Molecular follow up of the insertional
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Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
Data for the paper Hernandez et al 2021 https://doi.org/10.1016/j.ymthe.2020.09.030
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