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Cardiac Applications of CRISPR/AAV-Mediated Precise Genome Editing

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NIAID Data Ecosystem2026-05-02 收录
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https://www.ncbi.nlm.nih.gov/sra/SRP540824
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The activity of cardiomyocyte and control enhancers was assessed in mouse cardiomyocytes, using two assay formats: a Tnni1 genomically integrated MPRA and AAV-based episomal MPRAs with various minimal promoters. Overall design: AAV9 reporter pools were injected at P0 and tissue was harvested for measurement of enhancer activity at P28 by amplicon sequencing. See https://github.com/nvanduse/CASAAV-HDR_Applications for NGS processing scripts.
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2025-01-04
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