Mus musculus RNA-SEQ raw sequence reads. Mus musculus strain:FVB/N
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下载链接：
https://www.ncbi.nlm.nih.gov/bioproject/PRJNA305817
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资源简介：
We evaluated the therapeutic activity of the modified U1 particles in a mouse model affected by severe spinal muscular atrophy. ExSpeU1 introduced by germline transgenesis efficiently rescued the phenotype increasing SMN2 exon 7 splicing, SMN protein production and radically extending the life span.
创建时间：
2015-12-13
