Here, we report a virus-like recombinant biosome (reBiosome) as a safe and effective delivery vehicle for targeted gene therapy. A mutant biosome (mBiosome) was first prepared by genetically recombini

DataCite Commons2023-10-16 更新70

hazemessam/aav

基因治疗

生物学

--- license: afl-3.0 tags: - biology --- FLIP AAV Dataset Splits The AAV (Adeno-Associated Virus) dataset in FLIP focuses on predicting the fitness/efficiency of AAV capsid variants for gene therapy.

Hugging Face2026-01-02 更新110

Additional file 8 of Retinal organoids with X-linked retinoschisis RS1 (E72K) mutation exhibit a photoreceptor developmental delay and are rescued by gene augmentation therapy

基因治疗

视网膜疾病

Supplementary Material 8

DataCite Commons2024-08-15 更新80