Dataset from An Open-label Study to Evaluate Safety, Efficacy and Pharmacokinetics (PK) of Patisiran-LNP in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) With Disease Progression Post-Orthotopic Liver Transplant
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下载链接：
https://doi.org/10.25934/PR00008230
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资源简介：
The purpose of this study is to evaluate the efficacy, safety and pharmacokinetics of
patisiran in participants with hereditary transthyretin-mediated amyloidosis (hATTR
amyloidosis) with disease progression after liver transplant.
创建时间：
2025-07-07
