Foamy virus vector insertion junctions within murine-engrafted human LAD-1 HSPCs

NIAID Data Ecosystem2026-03-13 收录

载体整合位点

细胞基因治疗

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https://www.ncbi.nlm.nih.gov/bioproject/PRJNA785607 数据链接链接失效反馈

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资源简介：

To evaluate foamy virus vector insertion junctions within murine-engrafted human LAD-1 blood stem cells.

创建时间：

2021-12-02

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Recent preclinical investigations and clinical trials with stem cells mostly studied bone-marrow-derived mononuclear cells (BM-MNCs), which so far failed to meet clinically significant functional stud

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Foamy virus vector insertion junctions within murine-engrafted human LAD-1 HSPCs

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