The Myotubular and Centronuclear Myopathy Patient Registry (‘MTM and CNM Registry’) is an international database specific to these conditions, operated by Newcastle University in the UK as part of the
Abbreviations: ALD = alcohol associated liver disease, AP = alkaline phosphatase, NASH = non alcoholic steatohepatitis, m = male, f = female, y = yes, n = no, uk = unknown. Data are summarised as mean
The extended data includes: Team members listed, participant information sheets, consent forms and a list of attributes to be included in each Treatment Preference Methods.