We developed a comprehensive AmpliSeq panel for NGS analysis of EB and EI-asociated genomic loci. These included mutation hotspots and predicted off-target sites for gene editing agents. Some of the
Additional file 10: Table S8. Transcriptome profiles of HEK293T transfected of RfxCas13d, NeuN and crRNA (Linked to Response Fig. 8 of first revision).
We successfully develop a two-in-one approach to generate non-viral genome specific targeted CAR T cells through CRISPR/Cas9. In the adoptive therapy for relapsed/refractory aggressive B-cell non-Hodg
