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Additional file 1 of Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: a national French retrospective study

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Figshare2023-07-22 更新2026-04-08 收录
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https://springernature.figshare.com/articles/dataset/Additional_file_1_of_Effects_of_miglustat_therapy_on_neurological_disorder_and_survival_in_early-infantile_Niemann-Pick_disease_type_C_a_national_French_retrospective_study/23730943/1
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资源简介:
Additional file 1. Table S1: Clinical characteristics of patients with EI-NP-C.
提供机构:
Labarthe, François; Levade, Thierry; Freihuber, Cécile; Chabrol, Brigitte; Pichard, Samia; Dahmani-Rabehi, Bahia; Brassier, Anaïs; Sevin, Caroline; Vanier, Marie T.; Héron, Bénédicte; Broué, Pierre; Eyer, Didier; Latour, Philippe; Cances, Claude
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2023-07-22
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