Characteristics of included studies and identified prognostic indicators in DMD.

Figshare2022-03-25 更新2026-04-28 收录

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https://figshare.com/articles/dataset/Characteristics_of_included_studies_and_identified_prognostic_indicators_in_DMD_/19423245 数据链接链接失效反馈

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资源简介：

Characteristics of included studies and identified prognostic indicators in DMD.

创建时间：

2022-03-25

Data from: Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function

杜氏肌营养不良症

临床试验

Objective: We carried out first-in-patient studies of vamorolone, a first-in-class dissociative steroidal anti-inflammatory drug, in Duchenne muscular dystrophy. Methods: An open-label, multiple-asc

DataCite Commons2025-06-01 更新120

Mass-spectrometry results from fibroadipogenic progenitor cells isolated from healthy controls (n=3) and DMD patients (n=3)

蛋白质组学

杜氏肌营养不良症

Duchenne muscular dystrophy is a genetic disease produced by mutations in the dystrophin gene characterized by early onset muscle weakness leading to severe and irreversible disability. Muscle degener

DataCite Commons2025-03-25 更新90

German Portal for Medical Research Data

临床研究数据集成

多中心医学数据共享

The FDPG is the German Portal for Medical Research Data, a central online platform that allows researchers to request and access pseudonymized patient data and biosamples from routine clinical care at

知名数据库70

In vivo genome editing restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers [WES]

基因治疗疗效评估

杜氏肌营养不良症

Duchenne muscular dystrophy (DMD) is the most common fatal genetic disease. Clustered regularly interspaced short palindromic repeat (CRISPR)-mediated gene editing is a promising strategy for permanen

NIAID Data Ecosystem110

In vivo genome editing restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers [Nanopore sequencing]. In vivo genome editing restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers [Nanopore sequencing]

基因编辑

杜氏肌营养不良症

NIAID Data Ecosystem70