In vivo adenine base editing of mutant Galc gene ameliorates Krabbe disease progression
收藏NIAID Data Ecosystem2026-05-10 收录
下载链接：
https://www.ncbi.nlm.nih.gov/sra/SRP635121
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资源简介：
This project aims to validate the genome editing efficiency and off-target profiles of CRISPR-based base editors across in vitro cell models and in vivo systems. Amplicon sequencing was performed using Illumina platforms, and raw FASTQ files were deposited to support reproducibility of NGS-based off-target analysis.
创建时间：
2025-10-20
