Supplementary Material 2. Supplemental Fig. 1. a. Multidimensional scaling was used on raw data that had been log-transformed to visualize multidimensional proteomic distribution in two-dimensional sp
Niemann-Pick disease, type C1 (NPC1) is a fatal, neurodegenerative disorder for which there is no definitive therapy. In NPC1, a pathological cascade including neuroinflammation, oxidative stress and
Proteomic analysis using iTRAQ technique to identify global changes in Batten's disease samples using iPSCs derived from keratinocytes and differentiated to iNPCs Three separate mass spectrometry runs