Raw data obtained by Real time PCR performed to assess the expression of muscle-specific miRNAs, miR206, miR-133a, miR-133b, miR-1, in serum of 21 infantile SMA patients at baseline and after 6 months
Spinal muscular atrophy (SMA) is a monogenic disorder caused by loss of function mutations in the survival motor neuron 1 gene, which results in a broad range of disease severity, from neonatal to adu
