In vivo genome editing via CRISPR/Cas9 mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment

The raw sequencing data of targeted mouse genome and targeted transcripts in this article. The raw sequencing data of editing verification in edited RPE cells, iPSC and mouse retina tissues in this article.

本文所包含的原始测序数据包括：靶向小鼠基因组与靶向转录本的原始测序数据，以及编辑后的视网膜色素上皮（Retinal Pigment Epithelium, RPE）细胞、诱导多能干细胞（induced pluripotent stem cells, iPSC）和小鼠视网膜组织中编辑验证的原始测序数据。