dataset documenting article "Circulating MyomiRs as Potential Biomarkers to Monitor Response to Nusinersen in Pediatric SMA Patients"

Raw data obtained by Real time PCR performed to assess the expression of muscle-specific miRNAs, miR206, miR-133a, miR-133b, miR-1, in serum of 21 infantile SMA patients at baseline and after 6 months of nusinersen treatment.

本数据集为通过实时聚合酶链式反应（Real time PCR）获取的原始数据，用于评估21例婴儿型脊髓性肌萎缩症（Spinal Muscular Atrophy, SMA）患者在基线状态及接受诺西那生（nusinersen）治疗6个月后，其血清中肌肉特异性微RNA（miRNAs，包含miR206、miR-133a、miR-133b、miR-1）的表达水平。