Previously we have shown that compacted DNA nanoparticles can drive high levels of transgene expression after subretinal injection in the mouse eye. Here we delivered compacted DNA nanoparticles conta
This dataset contains the anonymized data used for all analyses in a study of OPA1-associated optic neuropathy in rhesus macaques. The Excel workbook All_data_Anonymized_25Nov25.xlsx includes multiple
Gene therapy constitutes one of the most promising mode of disease treatments. Two key properties for therapeutic delivery vectors are the transduction efficiency (how well the vector delivers therape
